NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's disease

Bibliographic Details
Main Author: Caria, Inês
Publication Date: 2024
Other Authors: Nunes, Maria João, Ciraci, Viviana, Carvalho, Andreia Neves, Ranito, Catarina, Santos, Susana G., Gama, Maria João, Castro-Caldas, Margarida, Rodrigues, Cecília M. P., Ruas, Jorge L., Rodrigues, Elsa
Format: Article
Language: eng
Source: Repositórios Científicos de Acesso Aberto de Portugal (RCAAP)
Download full: http://hdl.handle.net/10362/163059
Summary: Funding Information: The work was supported by FEDER/Programa Operacional Regional de Lisboa – Lisboa 2020 (LISBOA-01-0145-FEDER-030104) and by National funds from Fundação para a Ciência e a Tecnologia (PTDC/MEDFSL/30104/2017), and by the Swedish Research Council. Publisher Copyright: © 2023 The Authors
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spelling NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's diseaseBrain cholesterol metabolismLysosomesMitochondria dysfunctionNPC1Parkinson's diseaseMolecular MedicineMolecular BiologySDG 3 - Good Health and Well-beingFunding Information: The work was supported by FEDER/Programa Operacional Regional de Lisboa – Lisboa 2020 (LISBOA-01-0145-FEDER-030104) and by National funds from Fundação para a Ciência e a Tecnologia (PTDC/MEDFSL/30104/2017), and by the Swedish Research Council. Publisher Copyright: © 2023 The AuthorsDisruption of brain cholesterol homeostasis has been implicated in neurodegeneration. Nevertheless, the role of cholesterol in Parkinson's Disease (PD) remains unclear. We have used N2a mouse neuroblastoma cells and primary cultures of mouse neurons and 1-methyl-4-phenylpyridinium (MPP+), a known mitochondrial complex I inhibitor and the toxic metabolite of 1-methyl-4-phenyl-1,2,3,6-tetrahydropyridine (MPTP), known to trigger a cascade of events associated with PD neuropathological features. Simultaneously, we utilized other mitochondrial toxins, including antimycin A, oligomycin, and carbonyl cyanide chlorophenylhydrazone. MPP+ treatment resulted in elevated levels of total cholesterol and in a Niemann Pick type C1 (NPC1)-like phenotype characterized by accumulation of cholesterol in lysosomes. Interestingly, NPC1 mRNA levels were specifically reduced by MPP+. The decrease in NPC1 levels was also seen in midbrain and striatum from MPTP-treated mice and in primary cultures of neurons treated with MPP+. Together with the MPP+-dependent increase in intracellular cholesterol levels in N2a cells, we observed an increase in 5′ adenosine monophosphate-activated protein kinase (AMPK) phosphorylation and a concomitant increase in the phosphorylated levels of mammalian target of rapamycin (mTOR). NPC1 knockout delayed cell death induced by acute mitochondrial damage, suggesting that transient cholesterol accumulation in lysosomes could be a protective mechanism against MPTP/MPP+ insult. Interestingly, we observed a negative correlation between NPC1 protein levels and disease stage, in human PD brain samples. In summary, MPP+ decreases NPC1 levels, elevates lysosomal cholesterol accumulation and alters mTOR signaling, adding to the existing notion that PD may rise from alterations in mitochondrial-lysosomal communication.DCV - Departamento de Ciências da VidaUCIBIO - Applied Molecular Biosciences UnitRUNCaria, InêsNunes, Maria JoãoCiraci, VivianaCarvalho, Andreia NevesRanito, CatarinaSantos, Susana G.Gama, Maria JoãoCastro-Caldas, MargaridaRodrigues, Cecília M. P.Ruas, Jorge L.Rodrigues, Elsa2024-02-02T23:40:54Z2024-022024-02-01T00:00:00Zinfo:eu-repo/semantics/publishedVersioninfo:eu-repo/semantics/article16application/pdfhttp://hdl.handle.net/10362/163059eng0925-4439PURE: 81715012https://doi.org/10.1016/j.bbadis.2023.166980info:eu-repo/semantics/openAccessreponame:Repositórios Científicos de Acesso Aberto de Portugal (RCAAP)instname:FCCN, serviços digitais da FCT – Fundação para a Ciência e a Tecnologiainstacron:RCAAP2024-05-22T18:17:59Zoai:run.unl.pt:10362/163059Portal AgregadorONGhttps://www.rcaap.pt/oai/openaireinfo@rcaap.ptopendoar:https://opendoar.ac.uk/repository/71602025-05-28T17:48:23.717575Repositórios Científicos de Acesso Aberto de Portugal (RCAAP) - FCCN, serviços digitais da FCT – Fundação para a Ciência e a Tecnologiafalse
dc.title.none.fl_str_mv NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's disease
title NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's disease
spellingShingle NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's disease
Caria, Inês
Brain cholesterol metabolism
Lysosomes
Mitochondria dysfunction
NPC1
Parkinson's disease
Molecular Medicine
Molecular Biology
SDG 3 - Good Health and Well-being
title_short NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's disease
title_full NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's disease
title_fullStr NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's disease
title_full_unstemmed NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's disease
title_sort NPC1-like phenotype, with intracellular cholesterol accumulation and altered mTORC1 signaling in models of Parkinson's disease
author Caria, Inês
author_facet Caria, Inês
Nunes, Maria João
Ciraci, Viviana
Carvalho, Andreia Neves
Ranito, Catarina
Santos, Susana G.
Gama, Maria João
Castro-Caldas, Margarida
Rodrigues, Cecília M. P.
Ruas, Jorge L.
Rodrigues, Elsa
author_role author
author2 Nunes, Maria João
Ciraci, Viviana
Carvalho, Andreia Neves
Ranito, Catarina
Santos, Susana G.
Gama, Maria João
Castro-Caldas, Margarida
Rodrigues, Cecília M. P.
Ruas, Jorge L.
Rodrigues, Elsa
author2_role author
author
author
author
author
author
author
author
author
author
dc.contributor.none.fl_str_mv DCV - Departamento de Ciências da Vida
UCIBIO - Applied Molecular Biosciences Unit
RUN
dc.contributor.author.fl_str_mv Caria, Inês
Nunes, Maria João
Ciraci, Viviana
Carvalho, Andreia Neves
Ranito, Catarina
Santos, Susana G.
Gama, Maria João
Castro-Caldas, Margarida
Rodrigues, Cecília M. P.
Ruas, Jorge L.
Rodrigues, Elsa
dc.subject.por.fl_str_mv Brain cholesterol metabolism
Lysosomes
Mitochondria dysfunction
NPC1
Parkinson's disease
Molecular Medicine
Molecular Biology
SDG 3 - Good Health and Well-being
topic Brain cholesterol metabolism
Lysosomes
Mitochondria dysfunction
NPC1
Parkinson's disease
Molecular Medicine
Molecular Biology
SDG 3 - Good Health and Well-being
description Funding Information: The work was supported by FEDER/Programa Operacional Regional de Lisboa – Lisboa 2020 (LISBOA-01-0145-FEDER-030104) and by National funds from Fundação para a Ciência e a Tecnologia (PTDC/MEDFSL/30104/2017), and by the Swedish Research Council. Publisher Copyright: © 2023 The Authors
publishDate 2024
dc.date.none.fl_str_mv 2024-02-02T23:40:54Z
2024-02
2024-02-01T00:00:00Z
dc.type.status.fl_str_mv info:eu-repo/semantics/publishedVersion
dc.type.driver.fl_str_mv info:eu-repo/semantics/article
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dc.identifier.uri.fl_str_mv http://hdl.handle.net/10362/163059
url http://hdl.handle.net/10362/163059
dc.language.iso.fl_str_mv eng
language eng
dc.relation.none.fl_str_mv 0925-4439
PURE: 81715012
https://doi.org/10.1016/j.bbadis.2023.166980
dc.rights.driver.fl_str_mv info:eu-repo/semantics/openAccess
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reponame_str Repositórios Científicos de Acesso Aberto de Portugal (RCAAP)
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